Goals
- To fund research to cure Spinal Muscular Atrophy
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Overview
Spinal Muscular Atrophy is the number one genetic killer of children under two years old. Symptoms include severe weakness in the entire body. Babies are too weak to roll over, sit up, crawl. Children are too weak to stand or walk. Victims of SMA can lose head control, ability to swallow, ability to make facial expressions. Babies, kids and adults with Spinal Muscular Atrophy have weak lung capacity and which is often the cause of death. A common cold can lead to hospital stays and can cause a child to lose strength they never get back. The good news is that research is very promising. Researchers know the gene that causes SMA and the defective gene has a rare "back up" gene, that can be a source of therapy. These two facts makes SMA the neuromuscular disorder closet to a cure according to the National Institute of Health. So let's push SMA research over the finish line.
How will the 250K be Used? |
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| $ 250,000 | To fund a year of research |
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